On Wednesday, Google's DeepMind AI research lab announced AlphaGenome, an AI model designed to identify disease markers in large volumes of genetic data. It's badly needed in a field that has produced ...

Columnist Michael Le Page delves into a catalogue of hundreds of potentially beneficial gene mutations and variants that is ...

When you have a rare disease, managing doctor's appointments, prescriptions and care plans is difficult enough — figuring out ...

Gene therapy holds the promise of preventing and curing disease by manipulating gene expression within a patient's cells. However, to be effective, the new gene must make it into a cell's nucleus. The ...

This research 'holds promise for advancing studies on using pig livers to support or even replace human liver function,' says ...

Over the past four decades, rare disease drug development has evolved from a scientific aspiration into a central pillar of biopharmaceutical innovation. Regulatory reforms, scientific breakthroughs, ...

Vertex executives warned that Casgevy, its curative treatment for sickle cell disease, would be slow to reach patients. But ...

The Union Budget 2026-27 includes customs duty exemptions on drugs and medical foods used to treat seven rare diseases under ...

We recently compiled a list of the 20 Best Biotech Stocks Under $20 to Buy Now. Taysha Gene Therapies, Inc. is placed sixth on our list of best biotech stocks under $20. TheFly reported on January 5 ...

Drs Stephen Ward, CTO of Cell and Gene Therapy Catapult, and Annarita Miccio, managing director at Imagine Institute for Genetic Diseases, will lead the inaugural two-day event taking place at Hinxton ...

Detailed price information for Ultragenyx Pharmaceu (RARE-Q) from The Globe and Mail including charting and trades.