Cell and gene therapies use the body's building blocks - cells and genetic material - to boost the immune system or correct ...

An HIV-derived nucleoside therapy now treats rare genetic diseases by restoring mitochondrial DNA and improving muscle ...

In early January 2026, Bayer’s subsidiaries and partners reported a series of R&D advances, including FDA acceptance of ...

Gene therapy treatments for rare diseases are being developed, but getting them out of the lab has proved challenging.

Medscape Medical News talked with researcher Stacie Dusetzina about the prospects for a single-payer program to help with the ...

The ROAR trial tested the hypothesis that returning familial hypercholesterolemia-associated genetic results leads to ...

Cell and gene therapy are revolutionary approaches to treating diseases at the molecular level. They involve the manipulation ...

Expected rapid advances in CAR T and other cellular therapies may expand treatment options not only in cancer but also in ...

LEXINGTON, Mass. and AMSTERDAM, Jan. 09, 2026 (GLOBE NEWSWIRE) -- uniQure N.V. (NASDAQ: QURE), a leading gene therapy company advancing ...

But cell and gene therapies (CGTs) are catching up. During Cell and Gene Therapy International Europe 2025, held in Berlin, ...

Qure N.V. (NASDAQ:QURE) shares are popping on Friday after the company said the FDA will review the data package for AMT‑130, ...

Co-founded by Jennifer Doudna and Fyodor Urnov, the company intends to simultaneously develop many gene editing treatments ...