A new gene-editing therapy called Casgevy, which is designed to help treat patients suffering from sickle cell disease, has been endorsed by the National Catholic Bioethics Center and its president, ...

An HIV-derived nucleoside therapy now treats rare genetic diseases by restoring mitochondrial DNA and improving muscle ...

Cell and gene therapy are revolutionary approaches to treating diseases at the molecular level. They involve the manipulation ...

Cell and gene therapies use the body's building blocks - cells and genetic material - to boost the immune system or correct ...

Editor's note, May 20, 2024: In September 2022, Fred Hutch News covered a preprint describing the successful application in mice of a gene-editing strategy to cure herpes. Fred Hutch Cancer Center ...

An experimental gene therapy developed by researchers at UCLA, University College London and Great Ormond Street Hospital has restored and maintained immune system function in 59 of 62 children born ...

Boston biotech Beam Therapeutics has announced initial data from a phase 1/2 trial of its gene therapy for a genetic lung and liver disease, with no serious adverse events reported among the nine ...

Pfizer is pulling further away from the gene therapy field with its decision to discontinue hemophilia product Beqvez. The New York pharma is ending global development and commercialization of Beqvez ...

According to DataM Intelligence, the global cell and gene therapy market reached a value of US$13.90 billion in 2024 and is ...

Even hearing the phrase “Huntington’s disease” will make a room suddenly somber. So the joy that accompanied a recent announcement of results of an experimental gene therapy for the deadly diseases ...